Splicing modulation of ATXN2 as a therapeutic strategy to regulate Ataxin-2 protein levels in ALS
| Authors | Nicolette Heinsinger, Yi Wang, Steve Grauer, Zuo Zhang, Jacky Wong, Vladimir Simov, Marina Bukhtiyarova, Xi Ai, Craig Parish, Rebecca Meier Klein, Jason Uslaner, Sean Smith, Yuan Tian |
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| DOI | 10.1016/j.nbd.2026.107582 |
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| Source | View on PubMed |
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